An update on this film. Oscar nominee Mary McDonnell is nor the narrator. https://globalgenes.org/raredaily/actress-mary-mcdonnell-gives-voice-to-awareness-of-menkes-disease-in-new-film/ Her shar...
The chart below identifies 6 new FDA Products Receiving Orphan Designation for the week of 06/01 – 06/05/15 as of 06/07/15 in ascending “Orphan Drug Designation...
In reply to https://orphandruganaut.wordpress.com/2015/06/04/fda-breakthrough-therapy-and-a-rare-disease-genzymes-ert-olipudase-alfa-for-niemann-pick-disease/comment-page-1/#comment-8796
FDA Breakthrough Therapy And A Rare Disease: Genzyme’s ERT Olipudase Alfa For Niemann-Pick Disease.
FDA Breakthrough Therapy And A Rare Disease: Genzyme’s ERT Olipudase Alfa For Niemann-Pick Disease.
Reblogged this on DRUG REGULATORY AFFAIRS INTERNATIONAL.
Guest Blogger: 1st International Congress on Clinical Genetics And Genetic Counselling In Rare Disea….
In reply to jigsawtree. Thank you for your continuous supp...
When do we expect to see the 2015 issues we would love to read them can we expect to see a 10 year issue to enable groups to maybe purchase the information it is very helpful for patient groups t...
Reblogged this on urddad-foundation-blogroll and commented: We have always thou...
Reblogged this on urddad-foundation-blogroll.
Orphan drug companies have used with tremendous success as part of their drug life cycle management, the strategy to extend the life of their product by devising a succession of multiple discret...