Gene Therapy

Gene Therapy, Published online: 16 April 2024; doi:10.1038/s41434-024-00451-3 Long-term benefits of hematopoietic stem cell-based macrophage/microglia delivery of GDNF to the CNS in a mouse model...

https://www.nature.com/articles/s41434-024-00451-3

Gene Therapy, Published online: 02 April 2024; doi:10.1038/s41434-024-00450-4 A multinational survey of potential participant perspectives on ocular gene therapy

https://www.nature.com/articles/s41434-024-00450-4

Gene Therapy, Published online: 25 March 2024; doi:10.1038/s41434-024-00449-x Adeno-associated virus genome quantification with amplification-free CRISPR-Cas12a

https://www.nature.com/articles/s41434-024-00449-x

Gene Therapy, Published online: 22 March 2024; doi:10.1038/s41434-024-00448-y Precision ophthalmology: a call for Africa not to be left in the dark

https://www.nature.com/articles/s41434-024-00448-y

Gene Therapy, Published online: 14 March 2024; doi:10.1038/s41434-024-00446-0 Advancing rare disease treatment: EMA’s decade-long insights into engineered adoptive cell therapy for rare cancers...

https://www.nature.com/articles/s41434-024-00446-0

Gene Therapy, Published online: 12 March 2024; doi:10.1038/s41434-024-00447-z A shedding analysis after AAV8 CNS injection revealed fragmented viral DNA without evidence of functional AAV particl...

https://www.nature.com/articles/s41434-024-00447-z

Gene Therapy, Published online: 01 March 2024; doi:10.1038/s41434-024-00445-1 Are genetically modified protozoa eligible for ATMP status? Concerning the legal categorization of an oncolytic proto...

https://www.nature.com/articles/s41434-024-00445-1

Gene Therapy, Published online: 19 February 2024; doi:10.1038/s41434-024-00444-2 Analytical characterization of full, intermediate, and empty AAV capsids

https://www.nature.com/articles/s41434-024-00444-2